Unite with the rare disease community to create powerful partnerships, advance orphan therapeutics and deliver life-changing breakthroughs
The Rare Disease Summit connects key stakeholders to drive therapeutic progress, propel commercial strategies and inspire impactful advocacy. You’ll generate solution-focused approaches surrounding patient access, reimbursement, commercialization, launch, partnering and more, as you unify in areas of unmet medical need.
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Say Hello to Your Rare Disease Summit Leaders Council
Who can you expect meet at the Rare Disease Summit? Our Leaders Council is just the tip of the iceberg when it comes to the vast expertise our speaker lineup will bring. Prepare to meet these industry experts and so many more!
What's on Tap? Check Out Your Rare Disease 2025 Hot Topic Sneak Peek
We're hard at work developing the robust 2025 agenda – What can you expect? In this constantly evolving landscape, our industry experts will sharing their intel and expertise on the biggest challenges facing the rare disease industry. Your sneak peek includes:
FDA Updates on Rare Disease Product Development
Navigating the Complexities – The Evolving Pricing Landscape in Rare Diseases
Manufacturer Considerations for Building a Strategic Commercialization Plan
Cracking the Code – Investor Insights into Rare Disease Funding Opportunities
Utilizing AI Technology in a World of Zebras, Not Horses
Have a profound impact on the Rare Disease Community
While the industry has seen growth and heightened focus around the pursuit of orphan products and rare therapies, we’ve only scratched the surface. 2024 Attendees benefitted from high-impact content from experts from across the rare disease industry:
Innovative Approaches to Amplify Collaboration and Advancement
Uncover innovative solutions to issues alongside the top industry experts committed to shaping the future of Rare Disease
- Navigate FDA Updates on Rare Disease Product Development
- Helpful or Harmful – Using AI in the Rare Disease Space
- Unlocking Rare Disease Investment Success through Valuation, Risk and Innovation
- Innovation Called and Gene Therapy Answered
Riveting Keynotes and Ground-Breaking Panels to Deliver Fresh Perspectives
Join market leaders setting the stage for game-changing dialogue
- The Importance of Funding and Partnering from the Perspective of an Early Stage BioPharma Company
- Exploring the Terrain - Rare Disease Landscape from a Payer Perspective
- Thinking Outside the Box – Forming Unique Partnerships within Rare Disease
- Rare Caregivers Report—Experiences Supporting Loved Ones Living with Rare Diseases
A Collaborative Think Tank to Benchmark and Strategize on the Top Challenges in Rare Disease
The all-plenary design of this event enables for more meaningful interaction, higher level networking and closer up learning
- Hear multiple keynote addresses featuring key stakeholder perspectives, including Industry, Advocacy and Regulatory
- Have dedicated time to brainstorm with your peers on innovative ideas surrounding the different phases of Rare Disease Drug Development (ie. diagnosis, preclinical, drug development, regulatory)
- Engage in our Innovation Station to hear rapid fire presentations from the key innovators within the Rare Disease space
- Be able to take home with you new connections, new ideas and new best practices
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Rare Disease Innovation & Partnership Summit: Part of Access USA
Hundreds from the access community came together as three industry-leading events united under one roof for compelling discussions, industry benchmarking and extended networking. What happened? Click play to see event highlights and why you can't miss this pivotal access forum!
See Who You'll Meet at the Rare Disease Summit
You will benefit from attending this event if you work for a company that focuses on rare disease and orphan drugs and have responsibilities or involvement in the following areas:
Rare Disease
Orphan Drugs
Market Access
Commercial Strategy/Operations
Reimbursement
Early/Expanded Access
Launch Excellence
Product Launch
Portfolio Management/Strategy
Marketing
Development
Patient Advocacy
Payer Strategy
Patient Support/Services
This event will also benefit consultants and solution providers who provide services in the rare disease space.
Get the Latest Event Updates
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Connect and Network with Key Decision-Makers at the Rare Disease Summit
Whether you’re looking to generate quality leads, showcase thought leaders, or reinforce your brand, collaborate with us to identify custom sponsorship opportunities to help you reach your business objectives.
For more information about custom opportunities to reach a qualified audience, please contact us here.
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Outside vendors who contact you to sell attendee lists are operating independently and without approval of the event organizers.